2025 fourth_quarter Filing

FY 26 appropriations programmatic and report provisions pertaining to rare disease policy priorities; H.R. 1, budget reconciliation/One Big, Beautiful Bill Act.

Accelerating Kids Access to Care Act (H.R. 1509/S. 752) and related out-of-state Medicaid issues; Medicaid funding and budget reconciliation; H.R. 1, budget reconciliation/One Big, Beautiful Bill Act.

Implementation of FDA Rare Disease Innovation Hub; reauthorization of Pediatric Priority Review Voucher; reauthorization of Newborn Screening Saves Lives Act; Activities related to PDUFA VIII; Concerns about FDA Complete Response Letters and other issues related to rare disease therapies; Activities of Congressional Rare Disease Caucus.