2025 third_quarter Filing

Lobbying for continued funding from the government for rare disease research and development, including through the Rare Pediatric Disease Designation and Priority Review Voucher Programs; advocating for greater awareness about the rare disease community for doctors via the Give Kids a Chance Act.

Lobbying for continued funding from the government for rare disease research and development, including through the Rare Pediatric Disease Designation and Priority Review Voucher Programs; advocating for greater awareness about the rare disease community for doctors via the Give Kids a Chance Act.